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  2. What a $2 million per dose gene therapy reveals about drug ...

    www.aol.com/news/2-million-per-dose-gene...

    Elsewhere in the hospital, an infant — patient No. 1 in a landmark clinical trial — was receiving an IV infusion that, if it worked, would fix the genetic mutation that caused spinal muscular ...

  3. List of gene therapies - Wikipedia

    en.wikipedia.org/wiki/List_of_gene_therapies

    Alipogene tiparvovec (Glybera): AAV-based treatment for lipoprotein lipase deficiency (no longer commercially available); Axicabtagene ciloleucel (Yescarta): treatment for large B-cell lymphoma [1]

  4. List of clinical trial registries - Wikipedia

    en.wikipedia.org/wiki/List_of_clinical_trial...

    The DRKS is an open access, free of charge online register for clinical trials and is available both in English and German. DRKS is part of the WHO's ICTRP. The DRKS works with two partner registries in Germany, DeReG (German Registry for Somatic Gene-Transfer Trials) and Clinical Trial Registry of the University Medical Center Freiburg. [4]

  5. Altos Labs - Wikipedia

    en.wikipedia.org/wiki/Altos_Labs

    Altos Labs was formally started on 19 January 2022. [2] The name Altos Labs is based on the city of Los Altos in California. [2] The idea for Altos Labs originated with cell biologist and entrepreneur Richard D. Klausner, who co-founded the company with Hans Bishop.

  6. Voretigene neparvovec - Wikipedia

    en.wikipedia.org/wiki/Voretigene_neparvovec

    The gene therapy is not a cure for the condition, but substantially improves vision in those treated. [8] It is given as a subretinal injection. Voretigene neparvovec was approved for medical use in the United States in December 2017, [9] in Australia in August 2020, [10] in Canada in October 2020, [11] and in Switzerland in February 2020. [12].

  7. Gene therapy - Wikipedia

    en.wikipedia.org/wiki/Gene_therapy

    Clinical trials of gene therapy for sickle cell disease were started in 2014. [227] [228] In February LentiGlobin BB305, a gene therapy treatment undergoing clinical trials for treatment of beta thalassemia gained FDA "breakthrough" status after several patients were able to forgo the frequent blood transfusions usually required to treat the ...

  8. City of Hope National Medical Center - Wikipedia

    en.wikipedia.org/wiki/City_of_Hope_National...

    City of Hope is a private, non-profit clinical research center, hospital and graduate school located in Duarte, California, United States.The center's main campus resides on 110 acres (45 ha) of land adjacent to the boundaries of Duarte and Irwindale, with a network of clinical practice locations throughout Southern California, satellite offices in Monrovia and Irwindale, and regional ...

  9. Spark Therapeutics - Wikipedia

    en.wikipedia.org/wiki/Spark_Therapeutics

    Fidanacogene elaparvovec, previously known by its study ID number SPK-9001, [12] is a gene therapy for the treatment of hemophilia B. It was developed by Spark in partnership with Pfizer . Fidanacogene elaparvovec is an adeno-associated viral vector which is designed to transfer a working copy of the Factor IX gene into the livers of patients ...

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